A call to arms against ultra-rare diseases
نویسندگان
چکیده
The not-for profit foundation n-Lorem seeks to provide experimental antisense oligonucleotide treatments patients with ultra-rare disease free for their entire lifetime.
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ژورنال
عنوان ژورنال: Nature Biotechnology
سال: 2021
ISSN: ['1546-1696', '1087-0156']
DOI: https://doi.org/10.1038/s41587-021-00945-0